An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...

An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...

A new breakthrough in a rare genetic disease which causes children to age rapidly has been discovered using 'longevity genes' ...

Scientists have now created an encyclopedia of gene function for all known human genes that code for protein. This data uses the most current and reliable data, and it has also been released on a ...

A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain ...

The UB team that discovered how a gene found in 75% of us protects against neurodegeneration has now found that this same gene enhances immune function as well. The new findings were published in ...

Despite rapid advances in reading the genetic code of living organisms, scientists still face a major challenge today—knowing ...

“Beyond UniQure, the pipeline includes highly promising approaches that will ideally move the goal from merely managing ...

In a phase 2b trial, danicamtiv, a novel cardiac myosin activator, was well tolerated and associated with improved heart ...